BOY WITH RARE CONDITION AMAZES DOCTORS AFTER WORLD-FIRST GENE THERAPY

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Hunter syndrome is an inherited condition that causes progressive damage to the body and brain. The effects are sometimes described as a type of childhood dementia, and patients with the disease usually die before the age of 20 in the most severe cases. Medical staff in Manchester have halted the disease in a three-year-old boy by altering his cells using gene therapy. It has only been a year since starting the treatment, but the boy appears to be developing normally.